Emerging gene therapies for cystic fibrosis
نویسندگان
چکیده
منابع مشابه
Novel pharmacologic therapies for cystic fibrosis.
The Journal of Clinical Investigation | February 1999 | Volume 103 | Number 4 447 It has been nearly 10 years since the identification and cloning of the cystic fibrosis (CF) gene was announced (1). Despite rapid advances in our understanding of the molecular determinants of the disease, CF remains one of the most common lethal inherited autosomal recessive disorders in the Caucasian population...
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University of Pittsburgh, Swanson School of Engineering Submission Date 11.01.2016 1 Disclaimer—This paper partially fulfills a writing requirement for first year (freshman) engineering students at the University of Pittsburgh Swanson School of Engineering. This paper is a student, not a professional, paper. This paper is based on publicly available information and may not provide complete anal...
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Gene therapy for cystic fibrosis (CF) has been the subject of intense research over the last twenty-five years or more, using both viral and liposomal delivery methods, but so far without the emergence of a clinical therapy. New approaches to CF gene therapy involving recent improvements to vector systems, both viral and non-viral, as well as new nucleic acid technologies have led to renewed in...
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Background: Burkholderia pseudomallei is an important cause of acute fulminant pneumonia and septicaemia in tropical regions of northern Australia and south east Asia. Subacute and chronic forms of the disease also occur. There have been three recent reports of adults with cystic fibrosis (CF) who presumably acquired B pseudomallei infection during extended vacations or residence in either Thai...
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ژورنال
عنوان ژورنال: Expert Review of Respiratory Medicine
سال: 2019
ISSN: 1747-6348,1747-6356
DOI: 10.1080/17476348.2019.1634547